The Effect of Nusinersen Therapy on Laboratory Parameters of Patients with Spinal Muscular Atrophy.
Gamze Sarikaya UzanCem PaketçiÇağatay GünayPinar EdemÖzlem ÖzsoySemra Hız KurulUluç YişPublished in: Neuropediatrics (2022)
Our results support the safety and efficacy of nusinersen. However, changes in Cr levels according to the clinical type and treatment suggested that serum Cr could be a candidate marker for treatment follow-up.
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