Neurodevelopmental status and adaptive behavior of pediatric patients with mucopolysaccharidosis II: a longitudinal observational study.
Joseph MuenzerBarbara K BurtonHernan M AmartinoPaul R HarmatzLuis González Gutiérrez-SolanaMatilde Ruiz-GarciaYuna WuDavid MerbergDavid AlexanderianSimon A JonesPublished in: Orphanet journal of rare diseases (2023)
ClinicalTrials.gov, NCT01822184. Registered retrospectively: April 2, 2013.