Short term morphological rescue of the fovea after gene therapy with voretigene neparvovec.

Friederike Charlotte KortümMelanie KempfRonja JungSusanne KohlSaskia OttConstanze KortuemKrunoslav StingKatarina Stingl

Published in: Acta ophthalmologica (2021)

Rapid changes in the correlates of photoreceptor morphology after successful gene therapy in patients with LCA/EORD can be quantifiable on individual level.

Keyphrases

gene therapy