Gene Editing for CEP290 -Associated Retinal Degeneration.

Eric A PierceTomas S AlemanKanishka T JayasunderaBright S AshimateyKeunpyo KimAlia RashidMichael C JaskolkaRene L MyersByron L LamSteven T BaileyJason I ComanderAndreas K LauerAlbert M MaguireMark E Pennesi

Published in: The New England journal of medicine (2024)

and other genetic causes. (Funded by Editas Medicine and others; BRILLIANCE ClinicalTrials.gov number, NCT03872479.).

Keyphrases

optical coherence tomography
diabetic retinopathy
genome wide
optic nerve
copy number
dna methylation