Phase 3 Open-Label Clinical Trial of Elexacaftor/Tezacaftor/Ivacaftor in Children Aged 2 Through 5 Years with Cystic Fibrosis and at Least One F508del Allele.
Jennifer L GoralskiJordana E HoppeMarcus Alexander MallSusanna A McColleyEdward F McKoneBonnie RamseyJonathan H RaymentPhil RobinsonFlorian StehlingJennifer L Taylor-CousarElizabeth TullisNeil AhluwaliaAnna ChinChenghao ChuMengdi LuTao NiuTanya WeinstockFelix RatjenMargaret Rosenfeldnull nullPublished in: American journal of respiratory and critical care medicine (2023)
gov, ID: NCT04537793.