Development of a Mitochondrial Myopathy-Composite Assessment Tool.
Jean FlickingerJiaxin FanAmanda WellikRebecca GanetzkyAmy GoldsteinColleen C MurareskuAllan M GlanzmanElizabeth BallanceKristin LeonhardtElizabeth M McCormickBrianna SorethSara NguyenJennifer GornishIbrahim George-SankohJames PetersonLaura E MacMullenShailee VishnubhattMichael McBrideRichard HaasMarni J FalkRui XiaoZarazuela Zolkipli-CunninghamPublished in: JCSM clinical reports (2021)
We have developed and successfully validated a MM-specific Composite Assessment Tool to quantify the key domains of MM, shown to be abnormal in a Definite MM cohort. MM-COAST may hold particular utility as a meaningful outcome measure in future MM intervention trials.
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