Treatment of transfusion-dependent congenital dyserythropoietic anemia Type I patients with pegylated interferon alpha-2a.
Abed Abu-QuiderMahdi AslehHanna ShalevYariv FruchtmanMeriam Ben-HaroshGuy BeckJosef KapelushnikPublished in: European journal of haematology (2020)
Pegylated interferon α2a therapy is efficacious in CDA-I patients with a reasonable safety profile.