Double blind trial of a deuterated form of linoleic acid (RT001) in Friedreich ataxia.

David R LynchKatherine D MathewsSusan PerlmanTheresa ZesiewiczSub SubramonyOmid OmidvarAdam P VogelAna KrtolicaNadia LittermanLex van der PloegFrederic HeerinckxPeter MilnerMark Midei

Published in: Journal of neurology (2022)

The results of this study provide no evidence for a significant benefit of RT001 at the dosages tested in this Friedreich ataxia patient population.

Keyphrases

clinical trial
phase iii
study protocol
early onset
double blind
phase ii
case report
open label