L-2-hydroxyglutaric aciduria: a report of clinical, radiological, and genetic characteristics of two siblings from Egypt.
Abdel-Ghaffar Ismail FayedMohie-Eldin Tharwat MohamedElsayed AbedMostafa MeshrefAli Mahmoud AhmedPublished in: Neurocase (2024)
L-2-hydroxyglutaric aciduria (L-2-HGA) is a rare autosomal recessive disease characterized by elevated levels of hydroxyglutaric acid in the body fluids and brain with abnormal white matter. We present two siblings with psychomotor retardation and quadriparesis. Their brain imaging showed diffuse bilateral symmetrical involvement of the cerebral cortex, white matter, basal ganglia and cerebellum. The whole exome sequence studies revealed a homozygous likely pathogenic variant on chromosome 14q22.1 (NM_024884.2: c.178G > A; pGly60Arg) in the gene encoding for L-2-hydroxyglutarate dehydrogenase (L2HGDH) (OMIM #236792). Therefore, using the L2HGDH gene study is beneficial for L2HGA diagnosis.
Keyphrases
- white matter
- copy number
- genome wide
- multiple sclerosis
- intellectual disability
- high resolution
- dna methylation
- photodynamic therapy
- genome wide identification
- autism spectrum disorder
- functional connectivity
- gene expression
- low grade
- cerebral ischemia
- brain injury
- fluorescence imaging
- blood brain barrier
- muscular dystrophy
- genome wide analysis