PROTECT VIII Kids: BAY 94-9027 (PEGylated Recombinant Factor VIII) safety and efficacy in previously treated children with severe haemophilia A.

Elena Santagostino Gili Kenet Kathelijn FischerTina BissSanjay AhujaMacGregor Steele

Published in: Haemophilia : the official journal of the World Federation of Hemophilia (2020)

In PROTECT VIII Kids, which allowed tailoring of prophylaxis to individual clinical response, BAY 94-9027 was efficacious for bleed prevention and treatment in previously treated children with severe haemophilia A.

Keyphrases

young adults
early onset
recombinant human