Pharmacokinetic and Pharmacodynamic Properties of Cemdisiran, an RNAi Therapeutic Targeting Complement Component 5, in Healthy Subjects and Patients with Paroxysmal Nocturnal Hemoglobinuria.
Prajakta BadriXuemin JiangAnna BorodovskyNader NajafianJae KimValerie A ClausenVarun GoelBahru HabtemariamGabriel J RobbiePublished in: Clinical pharmacokinetics (2021)
NCT02352493.