Patient- and caregiver-reported impact of symptoms in Duchenne muscular dystrophy.

Spencer J RoseroJennifer WeinsteinJamison SeaburyAnika VarmaNuran DilekChristine ZizziMadeleine CoffeyBrittany GrecoJohn HeatwoleDanae AlexandrouDebra GuntrumEmma CiafaloniChad Heatwole

Published in: Muscle & nerve (2024)

There are many symptomatic themes that contribute to disease burden in individuals with DMD. These symptoms are identified by both individuals with DMD and their caregivers and have a variable level of importance and prevalence in the DMD population.

Keyphrases

duchenne muscular dystrophy
risk factors
muscular dystrophy
sleep quality
palliative care
case report