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Mortality and respiratory support in X-linked myotubular myopathy: a RECENSUS retrospective analysis.

Robert J GrahamFrancesco MuntoniImelda HughesSabrina W YumNancy L KuntzMichele L YangBarry J ByrneSuyash PrasadRachel AlvarezCasie A GenettiTmirah HaselkornEmma S JamesLaurie B LaRussoMojtaba NoursalehiSalvador RicoAlan H Beggs
Published in: Archives of disease in childhood (2019)
NCT02231697.
Keyphrases
  • cardiovascular events
  • late onset
  • risk factors
  • cardiovascular disease
  • type diabetes
  • coronary artery disease
  • myasthenia gravis