Mortality and respiratory support in X-linked myotubular myopathy: a RECENSUS retrospective analysis.
Robert J GrahamFrancesco MuntoniImelda HughesSabrina W YumNancy L KuntzMichele L YangBarry J ByrneSuyash PrasadRachel AlvarezCasie A GenettiTmirah HaselkornEmma S JamesLaurie B LaRussoMojtaba NoursalehiSalvador RicoAlan H BeggsPublished in: Archives of disease in childhood (2019)
NCT02231697.