Efficacy and safety of ruxolitinib in regularly transfused patients with thalassemia: results from a phase 2a study.
Ali T TaherZeynep KarakasElena CassinerioNoppadol SiritanaratkulAntonis KattamisAurelio MaggioStefano RivellaNorbert HollaenderBruyère MahuzierBrian GadbawYesim AydinokPublished in: Blood (2017)
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