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The vital role of natural history studies in rare disease: insights from X-linked dystonia parkinsonism.

Ihtsham Ul HaqAllison Brashear
Published in: Brain communications (2023)
This scientific commentary refers to 'Establishing a natural history of X-linked dystonia parkinsonism', by Acuna et al. (https://doi.org/10.1093/braincomms/fcad106).
Keyphrases
  • deep brain stimulation
  • parkinson disease
  • early onset
  • drug induced
  • case control