A Novel Metric for Predicting Severity of Disease Features in Friedreich's Ataxia.
Layne N RoddenChristian RummeySudha KesslerRobert B WilsonDavid R LynchPublished in: Movement disorders : official journal of the Movement Disorder Society (2023)
FRDA DB is a novel metric of disease severity that has utility in small datasets to demonstrate correlations that would not otherwise be evident with either GAA-TR or DD alone. This is important for discovering new biomarkers, as well as improving the prediction of severity of disease features in FRDA. © 2023 International Parkinson and Movement Disorder Society.
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