Vutrisiran: a new drug in the treatment landscape of hereditary transthyretin amyloid polyneuropathy.
Violaine Planté-BordeneuveValentine PerrainPublished in: Expert opinion on drug discovery (2024)
Vutrisiran offers a new treatment option for patients with ATTRv-PN. Vutrisian's easier delivery and administration route, at a quarterly frequency, as well as the absence of premedication, are major improvements to reduce patients' disease burden and improve their QoL. Its place in the therapeutic strategy is to be determined, considering affordability.