Spinal muscular atrophy: epidemiology and health burden in children - a Polish national healthcare database perspective before introduction of SMA-specific treatment.
Maria JędrzejowskaŁukasz NapiórkowskiKrystyna SzymańskaJoanna JędrzejczakMarcin RoszkowskiJerzy SłowińskiAnna FrączekDanuta RyglewiczBarbara WięckowskaPublished in: Neurologia i neurochirurgia polska (2021)
SMA caused significant mortality and morbidity in children. The National Health Fund database can be used to reliably record incident cases and track the care provided to paediatric SMA patients.
Keyphrases
- healthcare
- end stage renal disease
- young adults
- risk factors
- chronic kidney disease
- ejection fraction
- newly diagnosed
- public health
- emergency department
- cardiovascular disease
- intensive care unit
- palliative care
- adverse drug
- peritoneal dialysis
- health information
- cardiovascular events
- health insurance
- coronary artery disease
- combination therapy
- replacement therapy