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Crovalimab treatment in patients with paroxysmal nocturnal haemoglobinuria: Long-term results from the phase I/II COMPOSER trial.

Alexander RöthSatoshi IchikawaYoshikazu ItoJin Seok KimZsolt NagyNaoshi ObaraJens Peter PanseHubert SchrezenmeierSimona SicaJuliette SoretKensuke UsukiSung-Soo YoonNadiesh BalachandranMuriel BuriPontus LundbergHimika PatelKenji ShinomiyaAlexandre SostellyJun-Ichi Nishimura
Published in: European journal of haematology (2023)
Over a 3-year median treatment duration, crovalimab was well tolerated and sustained C5 inhibition was achieved. Intravascular haemolysis control, haemoglobin stabilisation and transfusion avoidance were maintained, signifying long-term crovalimab efficacy.
Keyphrases
  • blood pressure
  • clinical trial
  • study protocol
  • cardiac surgery
  • sickle cell disease