Gorham-Stout Syndrome of the Shoulder Girdle Successfully Controlled by Antiresorptive Agents: A Report of 2 Cases.
Takumi MatsumotoMasashi NaitoJun HiroseIzumi NakadaTeppei MorikawaSakae TanakaPublished in: JBJS case connector (2020)
These 2 cases suggest that antiresorptive agents targeting osteoclasts can be efficacious therapeutic options for GSD. This is the first case of GSD we are aware of which showed good response to denosumab treatment.