Dominant Distal Myopathy 3 (MPD3) Caused by a Deletion in the HNRNPA1 Gene.
Peter HackmanSalla M RusanenMridul JohariAnna ViholaPer Harald JonsonJaakko SarparantaKati DonnerPäivi LahermoSampo KoivunenHelena LuqueMerja SoininenIbrahim MahjnehMari AuranenMeharji ArumilliMarco SavareseBjarne UddPublished in: Neurology. Genetics (2021)
A small exon 10 deletion in the gene HNRNPA1 was identified as the cause of MPD3 in this family. The new HNRNPA1-related phenotype, upper limb presenting distal myopathy, was thus confirmed, and the family displays the complexities of gene identification.