A Promising Small Molecule for Vanishing White Matter Disease.

Divakar S MithalJennifer P Rubin

Published in: Pediatric neurology briefs (2018)

Investigators from Calico Life Sciences LLC and AbbVie report the effects of a novel drug targeting the genetic basis of Vanishing White Matter Disease (VWMD).

Keyphrases

white matter
small molecule
multiple sclerosis
emergency department
cancer therapy
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