Login / Signup

Highly efficient biallelic correction of homozygous COL7A1 mutation using ABE8e adenine base editor.

Imogen R BrooksYara AlrokhAidin KazemizadehKatarzyna BalonGregory NewbyDavid R LiuŁukasz ŁaczmańskiJohn A McGrathJoanna Jackow-Malinowska
Published in: The British journal of dermatology (2024)
Keyphrases
  • highly efficient
  • intellectual disability