Outcomes and outcome measures.

Giancarlo CastamanVictor Jimenez-YusteSamanta GouwRoseline d'Oiron

Published in: Haemophilia : the official journal of the World Federation of Hemophilia (2024)

How incorporating these outcome measures in the process of approval of novel treatments for these disorders by regulatory authorities remains to be established.

Keyphrases

transcription factor
drug administration
adipose tissue
metabolic syndrome
skeletal muscle
insulin resistance
weight loss