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Tandem hematopoietic stem cell transplant considerations in families with multiple siblings affected by DOCK8 deficiency.

Sara SilbertKristen ColeSima Z BedoyaAlexandra F FreemanJennifer S WhangboDaniele N AvilaHelen C SuBonnie YatesMonica EpsteinDavid S WendlerSung-Yun PaiDennis D HicksteinLori WienerNirali N Shah
Published in: Bone marrow transplantation (2022)
Keyphrases
  • hematopoietic stem cell
  • intellectual disability