Results of a randomized double-blind study evaluating luvadaxistat in adults with Friedreich ataxia.

Hao WangJonathan NortonLin XuNicholas DeMartinisRohini SenAnkit ShahJennifer FarmerDavid R Lynch

Published in: Annals of clinical and translational neurology (2021)

Luvadaxistat was safe and well tolerated in this cohort of adults with FRDA; however, it did not demonstrate efficacy as a treatment for this condition.

Keyphrases

double blind
clinical trial
early onset
study protocol
replacement therapy