European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience.

Ans T van der PloegM E KruijshaarA ToscanoP LaforêtC AngeliniR H LachmannS I Pascual PascualM RobertsK RöslerT StulnigP A van DoornP Y K Van den BerghJ VissingB Schosernull null

Published in: European journal of neurology (2017)

This is the first European consensus recommendation for starting and stopping ERT in adult patients with Pompe disease, based on the extensive experience of experts from different countries.

Keyphrases

replacement therapy
smoking cessation
late onset
clinical practice