Patient preferences for gene therapy in haemophilia: Results from the PAVING threshold technique survey.

Eline van OverbeekeBrett HauberSissel MichelsenKathelijne PeerlinckCatherine Marie Lambert Cedric HermansPhu Quoc LêMichel GoldmanSteven SimoensIsabelle Huys

Published in: Haemophilia : the official journal of the World Federation of Hemophilia (2021)

Results from this study proved the value of educating patients on novel treatments. Moreover, preference heterogeneity for novel treatments was confirmed in this study. In gene therapy decision-making, preference heterogeneity and the impact of patient education on acceptance should be considered.

Keyphrases

gene therapy
decision making
end stage renal disease
single cell
newly diagnosed
quality improvement
patient reported outcomes
patient reported