Fabry-specific treatment in Australia: time to align eligibility criteria with international best practices.
Kathleen M NichollsCharles DenaroMichel C TchanCarolyn Jane EllawayDrago BratkovicSheridan CampbellMegan FookesMark ThomasPublished in: Internal medicine journal (2024)
Australian access criteria are misaligned with current clinical evidence. The clinical statements and proposed classification and initiation criteria should prompt discussions to support more equitable access to treatment and better align Australian practice with contemporary evidence and international guidelines.