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Efficacy of Lomitapide in the Treatment of Familial Homozygous Hypercholesterolemia: Results of a Real-World Clinical Experience in Italy.

Laura D'ErasmoAngelo Baldassare CefalùDavide NotoAntonina GiammancoMaurizio AvernaPaolo PintusPaolo MeddeGiovanni Battista VignaCesare SirtoriLaura CalabresiChiara PavanelloMarco BucciCarlo SabbàPatrizia SuppressaFrancesco NatalePaolo CalabròTiziana SampietroFederico BigazziFrancesco SbranaKatia BonomoFulvio SileoMarcello Arca
Published in: Advances in therapy (2017)
In this real-world experience, lomitapide was confirmed to be a very powerful cholesterol-lowering agent in HoFH showing a good safety profile.
Keyphrases
  • low density lipoprotein
  • combination therapy