Positive Impact of Home ERT for Mucopolysaccharidoses and Pompe Disease: The Lesson Learnt from the COVID-19 Pandemic.

Agata FiumaraGiuseppina LanzafameAnnamaria Sapuppo Alessia ArenaLara CirnigliaroRita Barone

Published in: Healthcare (Basel, Switzerland) (2023)

Home ERT leads to a clear improvement in "daily life skills", as represented in our by sample by positive feelings, better emotional self-control, and an increased ability to understand the feelings of relatives. Our data underline the paramount positive effect home ERT has on both patients and their families.

Keyphrases

healthcare
end stage renal disease
ejection fraction
newly diagnosed
late onset
chronic kidney disease
machine learning
prognostic factors
patient reported outcomes
physical activity
electronic health record