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Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency.

Alessandra MagnaniJean-Marie JouannicJérémie RosainAurélie GabrionFabien TouzotCécile RoudautSven KrackerNizar MahlaouiAntoine ToubertEmmanuel ClaveElisabeth A MacintyreIsabelle Radford-WeissMarion AlcantaraElisa MagrinBrigitte TernauxJennifer NisoyLaure CaccavelliAnne-Marie DarrasCapucine PicardStéphane BlancheMarina Cavazzana
Published in: Blood advances (2020)
Keyphrases
  • stem cell transplantation
  • high dose
  • early onset
  • drug induced