Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency.
Alessandra MagnaniJean-Marie JouannicJérémie RosainAurélie GabrionFabien TouzotCécile RoudautSven KrackerNizar MahlaouiAntoine ToubertEmmanuel ClaveElisabeth A MacintyreIsabelle Radford-WeissMarion AlcantaraElisa MagrinBrigitte TernauxJennifer NisoyLaure CaccavelliAnne-Marie DarrasCapucine PicardStéphane BlancheMarina CavazzanaPublished in: Blood advances (2020)