Assessing validity of the EQ-5D-5L proxy in children and adolescents with Duchenne muscular dystrophy or spinal muscular atrophy.
Richard Huan XuYi DaiShamay S M NgHector W H TsangShuyang ZhangDong DongPublished in: The European journal of health economics : HEPAC : health economics in prevention and care (2023)
Based on the measurement properties assessed in this study, the EQ-5D-5L proxy is a valid and reliable tool for measuring the health-related quality of life of individuals with DMD or SMA rated by caregivers. Further studies should examine the content validity of the EQ-5D as well as the performance of its young version in these two patient groups.