Therapeutic indications and metabolic effects of metreleptin in patients with lipodystrophy syndromes: Real-life experience from a national reference network.
Héléna MosbahMarie-Christine VantyghemEstelle NobécourtFabrizio AndreelliFrancoise ArchambeaudElise BismuthClaire BrietMaryse CartignyBenjamin ChevalierBruno DonadilleAnne DaguenelMathilde FichetJean-François GautierSonja JanmaatIsabelle JéruCarole LegagneurLysiane LeguierJulie MaitreElise MongeoisChristine PoitouPr Eric RenardYves ReznikAnne SpiteriFlorence TravertBruno VergèsJamila ZammouriCorinne VigourouxCamille VatierPublished in: Diabetes, obesity & metabolism (2022)
In this real-life setting study, metabolic outcomes are improved by metreleptin therapy in patients with GLD. The therapeutic indication for metreleptin needs to be clarified in patients with PLD.