A novel integrative multi-omics approach to unravel the genetic determinants of rare diseases with application in sinusoidal obstruction syndrome.
Nicolas WaespeSimona Jurkovic MlakarIsabelle DupanloupMohamed Aziz RezguiHenrique BittencourtMaja KrajinovicClaudia Elisabeth KuehniTiago NavaMarc AnsariPublished in: PloS one (2023)
For the clinical dataset: Clinicaltrials.gov: NCT01257854. https://clinicaltrials.gov/ct2/history/NCT01257854.