Outcomes and outcome measures.

Giancarlo Castaman Victor Jimenez YusteSamanta GouwRoseline d'Oiron

Published in: Haemophilia : the official journal of the World Federation of Hemophilia (2024)

How incorporating these outcome measures in the process of approval of novel treatments for these disorders by regulatory authorities remains to be established.

Keyphrases

transcription factor
drug administration
type diabetes
metabolic syndrome
adipose tissue