Carglumic acid in methylmalonic acidemia: Use of breast milk as an alternative vehicle to water.

Héctor C García-Díaz Carlos Javier Parramon-TeixidóSusana Clemente-BatistaInés Jiménez-LozanoAlicia Montaner RamonMireia Del Toro

Published in: Journal of clinical pharmacy and therapeutics (2022)

BM as a vehicle for NCG is a safe and effective option for patients who refuse suspension in water and could lead to better treatment compliance in paediatric patients.

Keyphrases

end stage renal disease
ejection fraction
newly diagnosed
chronic kidney disease
intensive care unit
emergency department
prognostic factors
patient reported outcomes