Small molecule drug development for rare genodermatoses - evaluation of the current status in epidermolysis bullosa.

Verena WallyManuela ReisenbergerSophie KitzmüllerMartin Laimer

Published in: Orphanet journal of rare diseases (2020)

We provide a comprehensive summary of the current status of clinical small molecule development for EB and discuss prospects and limitations in orphan drug development for rare conditions like EB.

Keyphrases

current status
small molecule
protein protein