David A Smith (Dave Smith, David Smith)

Publication Activity (10 Years)

Years Active: 2017-2023
Publications (10 Years): 7

Top Topics

Top Venues

Wellcome open research

Journal of clinical medicine

This page only lists publications with an associated author ORCID identifier.

Publications

Michael Paul Hughes, Hemanth Ramesh Nelvagal, Oliver Coombe-Tennant, David A Smith, Claire Smith, Giulia Massaro, Laura Poupon-Bejuit, Frances Mary Platt, Ahad Abdul Rahim
A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann-Pick Type C1 Disease. Cells 12 (12) (2023)
Michael Paul Hughes, Hemanth Ramesh Nelvagal, Oliver Coombe-Tennant, David A Smith, Claire Smith, Giulia Massaro, Laura Poupon-Bejuit, Frances Mary Platt, Ahad Abdul Rahim
A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann-Pick Type C1 Disease. Cells 12 (12) (2023)
Michael Paul Hughes, Hemanth Ramesh Nelvagal, Oliver Coombe-Tennant, David A Smith, Claire Smith, Giulia Massaro, Laura Poupon-Bejuit, Frances Mary Platt, Ahad Abdul Rahim
A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann-Pick Type C1 Disease. Cells 12 (12) (2023)
Isabelle Williams, Sumeet Pandey, Wolfram Haller, Hien Quoc Huynh, Alicia Chan, Gesche Düeker, Ruth Bettels, Laurent Peyrin-Biroulet, Chinenye R Dike, Catherine DeGeeter, David A Smith, Nada Al Eisa, Nick Platt, Thorsten Marquardt, Tobias Schwerd, Frances Mary Platt, Holm H Uhlig
Anti-TNF therapy for inflammatory bowel disease in patients with neurodegenerative Niemann-Pick disease Type C. Wellcome open research 7 (2022)
Oscar C W Chen, Stephan Siebel, Alexandria Colaco, Elena-Raluca Nicoli, Nick Platt, Dawn Shepherd, Stephanie Newman, Andrew E Armitage, Nicole Y Farhat, George Seligmann, Claire Smith, David A Smith, Alaa Abdul-Sada, Mylvaganam Jeyakumar, Hal Drakesmith, Forbes D Porter, Frances Mary Platt
Defective iron homeostasis and hematological abnormalities in Niemann-Pick disease type C1. Wellcome open research 7 (2022)
Ecem Kaya, David A Smith, Claire Smith, Barry Boland, Michael Strupp, Frances Mary Platt
Beneficial Effects of Acetyl-DL-Leucine (ADLL) in a Mouse Model of Sandhoff Disease. Journal of clinical medicine 9 (4) (2020)
Elena-Raluca Nicoli, Mylene Huebecker, David A Smith, Lauren Morris, Frances Mary Platt
Differential response of the liver to bile acid treatment in a mouse model of Niemann-Pick disease type C. Wellcome open research 2 (2017)