Manuel A F V Gonçalves

Loop profile ORCID

Publication Activity (10 Years)

Years Active: 2017-2024
Publications (10 Years): 11

Top Venues

Nucleic acids research

Cells

Journal of inherited metabolic disease

Journal of medical genetics

Universiteit Leiden

Universidade de Lisboa Faculdade de Ciências (MSC)

This page only lists publications with an associated author ORCID identifier.

Affiliation History

Universiteit Leiden

Netherlands

Associate professor :: Cell and Chemical Biology - Leiden University Medical Centre

Education History

Universidade de Lisboa Faculdade de Ciências Jun 15 1991 - Jun 15 1996

Portugal

MSC

Publications

Qian Wang, Sabrina Capelletti, Jin Liu, Josephine M Janssen, Manuel A F V Gonçalves
Selection-free precise gene repair using high-capacity adenovector delivery of advanced prime editing systems rescues dystrophin synthesis in DMD muscle cells. Nucleic acids research 52 (5) (2024)
Qian Wang, Sabrina Capelletti, Jin Liu, Josephine M Janssen, Manuel A F V Gonçalves
Selection-free precise gene repair using high-capacity adenovector delivery of advanced prime editing systems rescues dystrophin synthesis in DMD muscle cells. Nucleic acids research (2024)
Qian Wang, Sabrina Capelletti, Jin Liu, Josephine M Janssen, Manuel A F V Gonçalves
Selection-free precise gene repair using high-capacity adenovector delivery of advanced prime editing systems rescues dystrophin synthesis in DMD muscle cells. Nucleic acids research 52 (5) (2024)
Qian Wang, Jin Liu, Josephine M Janssen, Manuel A F V Gonçalves
Precise homology-directed installation of large genomic edits in human cells with cleaving and nicking high-specificity Cas9 variants. Nucleic acids research (2023)
Francesca Tasca, Marcella Brescia, Qian Wang, Jin Liu, Josephine M Janssen, Karoly Szuhai, Manuel A F V Gonçalves
Large-scale genome editing based on high-capacity adenovectors and CRISPR-Cas9 nucleases rescues full-length dystrophin synthesis in DMD muscle cells. Nucleic acids research 50 (13) (2022)
Qian Wang, Jin Liu, Josephine M Janssen, Francesca Tasca, Hailiang Mei, Manuel A F V Gonçalves
Broadening the reach and investigating the potential of prime editors through fully viral gene-deleted adenoviral vector delivery. Nucleic acids research 49 (20) (2021)
Francesca Tasca, Qian Wang, Manuel A F V Gonçalves
Adenoviral Vectors Meet Gene Editing: A Rising Partnership for the Genomic Engineering of Human Stem Cells and Their Progeny. Cells 9 (4) (2020)
Hidde A Zittersteijn, Manuel A F V Gonçalves, Wytske M van Weerden
A primer to gene therapy: Progress, prospects, and problems. Journal of inherited metabolic disease 44 (1) (2020)
Marcella Brescia, Josephine M Janssen, Jin Liu, Manuel A F V Gonçalves
High-Capacity Adenoviral Vectors Permit Robust and Versatile Testing of DMD Gene Repair Tools and Strategies in Human Cells. Cells 9 (4) (2020)
Remko Goossens, Marlinde L van den Boogaard, Richard J L F Lemmers, Judit Balog, Patrick J van der Vliet, Iris M Willemsen, Julie Schouten, Ignazio Maggio, Nienke van der Stoep, Wytske M van Weerden, Stephen J Tapscott, Niels Geijsen, Manuel A F V Gonçalves, Sabrina Sacconi, Rabi Tawil, Silvère M van der Maarel
Intronic SMCHD1 variants in FSHD: testing the potential for CRISPR-Cas9 genome editing. Journal of medical genetics 56 (12) (2019)
Xiaoyu Chen, Josephine M Janssen, Jin Liu, Ignazio Maggio, Anke E J 't Jong, Harald M M Mikkers, Manuel A F V Gonçalves
In trans paired nicking triggers seamless genome editing without double-stranded DNA cutting. Nature communications 8 (1) (2017)

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Publication Activity (10 Years)

Top Topics

Top Venues

Manuel A F V Gonçalves