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An LNP-CRISPR gene editing drug demonstrates efficacy and safety in patients with hereditary angioedema following in vivo administration.

Norbert PardiZoltán Ivics
Published in: The Journal of allergy and clinical immunology (2024)
Keyphrases
  • genome editing
  • crispr cas
  • genome wide
  • angiotensin converting enzyme
  • adverse drug
  • emergency department
  • drug induced
  • angiotensin ii