Human umbilical cord mesenchymal stem cell-based gene therapy for hemophilia B using scAAV-DJ/8-LP1-hFIXco transduction.
Zibin BuJintu LouWeiqun XuLingyan ZhangYong-Min TangPublished in: Stem cell research & therapy (2024)
We have discovered a novel and safer HUCMSCs mediated approach potentially effective for gene therapy in hemophilia B.