Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table.
Glenn F PierceK John PasiDonna CoffinRadoslaw KaczmarekDavid LillicrapJohnny N MahlanguDawn RottelliniThomas SanniéAlok SrivastavaThierry VandenDriesscheAlain Weillnull nullPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2020)
This issue of ideal and acceptable factor level expression and other unresolved issues will be brought to the 3rd WFH GTRT in 2020.