Elexacaftor/tezacaftor/ivacaftor in children aged 6-11 years with cystic fibrosis, at least one F508DEL allele, and advanced lung disease: A 24-week observational study.
Donatello SalvatoreGiuseppe CiminoPatrizia TroianiElisabetta BignaminiIrene EspositoGiuseppina LeonettiMaurizio ZandaDaniela ManunzaAngela PepePublished in: Pediatric pulmonology (2022)