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Elexacaftor/tezacaftor/ivacaftor in children aged 6-11 years with cystic fibrosis, at least one F508DEL allele, and advanced lung disease: A 24-week observational study.

Donatello SalvatoreGiuseppe CiminoPatrizia TroianiElisabetta BignaminiIrene EspositoGiuseppina LeonettiMaurizio ZandaDaniela ManunzaAngela Pepe
Published in: Pediatric pulmonology (2022)
Keyphrases
  • cystic fibrosis
  • young adults
  • randomized controlled trial
  • study protocol
  • double blind