Oral tetrahydrouridine and decitabine for non-cytotoxic epigenetic gene regulation in sickle cell disease: A randomized phase 1 study.
Robert MolokieDonald LavelleMichel GowhariMichael PaciniLani KrauzJohara HassanVinzon IbanezMaria A RuizKwok Peng NgPhilip WoostTomas RadivoyevitchDaisy PacelliSherry FadaMatthew RumpMatthew M HsiehJohn F TisdaleJames JacobbergerMitch A PhelpsJames Douglas EngelSanthosh SarafLewis L HsuVictor GordeukJoseph DeSimoneYogen SaunthararajahPublished in: PLoS medicine (2017)
ClinicalTrials.gov, NCT01685515.