Landmark endorsement of a global registry: The European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP), publicly endorses World Federation of Hemophilia Gene Therapy Registry as global standard.
Barbara A KonkleFlora PeyvandiDonna CoffinMayss NaccacheToong YouttananukornGlenn F Piercenull nullPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2023)