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Associations Between Variant Repeat Interruptions and Clinical Outcomes in Myotonic Dystrophy Type 1.

Stephan WenningerSarah A CummingKristina GutschmidtKees OkkersenAura Cecilia Jimenez-MorenoFerroudja DaidjHanns LochmüllerFiona HogarthHans KnoopGuillaume BassezDarren G MoncktonBaziel G M van EngelenBenedikt Schoser
Published in: Neurology. Genetics (2021)
ClinicalTrials.gov NCT02118779.
Keyphrases
  • early onset
  • muscular dystrophy