Long-Term Impact of Lumacaftor/Ivacaftor Treatment on Cystic Fibrosis Disease Progression in Children 2 Through 5 Years of Age Homozygous for F508del-CFTR : A Phase 2, Open-Label Clinical Trial.
Mirjam StahlJobst RoehmelMonika EichingerFelix DoellingerLutz NaehrlichMatthias V KoppAnna-Maria DittrichOlaf SommerburgPartha RayAnita ManiktalaTu XuSarah ConnerAniket JoshiMolly MasciaMark Oliver WielpützMarcus Alexander MallPublished in: Annals of the American Thoracic Society (2024)
gov, ID: NCT03625466.