Efficacy and safety of avatrombopag in combination with immunosuppressive therapy in treatment-naïve and relapsed/refractory severe aplastic anaemia: protocol for the DIAAMOND-Ava-FIRST and DIAAMOND-Ava-NEXT Bayesian Optimal Phase II trials.
Zoe K McQuiltenStephane HeritierLucy FoxVanessa FoxLauren YoungPiers BlomberyIlona CunninghamJennifer CurnowAlisa HigginsDevendra K HiwaseRobin FilshieFrank FirkinPaul LacazeKylie MasonAnthony K MillsDominic PepperellSushrut PatilWilliam StevensonJeff SzerNeil WatersKate WilsonStephen TingErica WoodPublished in: BMJ open (2024)
ACTRN12619001042134, ACTRN12619001043123.
Keyphrases
- phase ii
- clinical trial
- open label
- acute lymphoblastic leukemia
- randomized controlled trial
- acute myeloid leukemia
- diffuse large b cell lymphoma
- allogeneic hematopoietic stem cell transplantation
- multiple myeloma
- phase iii
- double blind
- combination therapy
- placebo controlled
- stem cells
- drug induced
- replacement therapy