Real-world effectiveness of voxelotor for treating sickle cell disease in the US: a large claims data analysis.

Nirmish ShahThokozeni LipatoOfelia AlvarezThomas DeleaAlexander Lonshteyn Derek WeyckerAndy NguyenAnne BeaubrunIrene Agodoa

Published in: Expert review of hematology (2022)

These data align with randomized controlled trial results showing voxelotor improvements and support that voxelotor may lower transfusion and VOC rates in clinical practice.

Keyphrases

sickle cell disease
data analysis
randomized controlled trial
clinical practice
study protocol
health insurance
systematic review
electronic health record
big data
machine learning
acute kidney injury
cardiac surgery
artificial intelligence
deep learning